Brain disease treated by gene therapy – A treatment based on HIV finds first success in…
A treatment based on HIV finds first success in humans.Researchers have halted a fatal brain disease by delivering a therapeutic gene to the stem cells that mature into blood cells. The gene was transferred using a virus derived from HIV, a technique that researchers have pursued for more than a decade but has not been successful in humans until now. Together with his colleagues, paediatric neurologist Patrick Aubourg at INSERM — France's main biomedical research agency — and at the Saint-Vincent de Paul Hospital in Paris, developed the system to treat X-linked adrenoleukodystrophy (ALD), a neurodegenerative disease that affects young...
Original Article: Forum: News/Activism
Tags: Biomedical Research Agency, Blood Cells, Colleagues, Decade, Fatal Brain Disease, Gene Therapy, Hiv, Hiv Treatment, Inserm, Neurodegenerative Disease, Neurologist, Paris, Saint Vincent De Paul, Saint Vincent De Paul Hospital, Stem Cells, Therapeutic Gene, Vincent De Paul, Virus Hiv, X27, X97